uniQure presents Fabry gene therapy safety updates at SSIEM 2026
Representatives shared clinical findings at the European conference in Helsinki, fostering discussions with researchers about future therapeutic strategies for the metabolic disorder.
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Gene therapy company targeting neurological and rare diseases
uniqure.comLast updated
In short: uniQure submitted regulatory applications for its Huntington's gene therapy AMT-130 following a favorable policy shift by the FDA.
Representatives shared clinical findings at the European conference in Helsinki, fostering discussions with researchers about future therapeutic strategies for the metabolic disorder.
The Lexington office welcomed two University of Buffalo experts who shared clinical insights for improving patient management during the event.
The company filed a Biologics License Application with the U.S. FDA and a Marketing Authorisation Application with the United Kingdom’s MHRA for potential treatment of Huntington’s disease.
Executive Director Steven Casto will share findings on the gene therapy candidate during the September event in Medellin, Colombia.
Before the end of September, UniQure is expected to report four-year results from the closely tracked clinical trial of its gene therapy for Huntington’s disease.
On September 2, 2026, William Blair reinstated coverage on uniQure (QURE) with a rating of...
Uniqure stock wavered Wednesday after the FDA accepted its application.
Dutch gene therapy developer uniQure said on Wednesday it had applied for U.S. approval of its exper...
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