CRISPR Therapeutics expands FDA approval for young children
It is the first gene-edited therapy approved for children this young, covering both sickle cell disease and beta thalassemia.
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Gene-editing therapeutics developer
crisprtx.comLast updated
In short: CRISPR Therapeutics secured expanded FDA approval for Casgevy in young children and reported strong revenue growth for the therapy.
It is the first gene-edited therapy approved for children this young, covering both sickle cell disease and beta thalassemia.
Revenue included $43M from CASGEVY, cash increased to $2.44B, and development milestones advanced across pipeline.
The notes due 2031 will be offered to qualified institutional buyers in a private offering.
CASGEVY generated $116M in 2025 revenue, with 64 patient infusions, and pipeline advances in autoimmune, oncology, and in vivo programs.
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