Ultragenyx competitors

View the competitive landscape for Ultragenyx, featuring companies like Ionis, Vertex Pharmaceuticals, and BioMarin. Mapping a different industry? Browse our competitor database or generate a competitor list for any company.

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Ultragenyx

Biopharmaceutical company developing treatments for rare and ultrarare genetic diseases

ultragenyx.com

List of Ultragenyx competitors

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    Ionis

    Biotechnology company developing RNA-targeted therapeutics for rare diseases

    ionis.com
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    Vertex Pharmaceuticals

    Biopharmaceutical company developing medicines for serious genetic diseases

    vrtx.com
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    BioMarin

    Biopharmaceutical company developing therapies for rare genetic diseases

    biomarin.com
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    BridgeBio

    Biopharmaceutical company developing therapies for various genetic diseases

    bridgebio.com
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    bluebird bio

    Biotechnology company developing gene therapies for severe genetic diseases

    genetixbiotx.com
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    Amicus Therapeutics

    Biotechnology company focused on treatments for rare metabolic diseases

    amicusrx.com
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    PTC Therapeutics

    Biopharmaceutical company developing treatments for rare genetic disorders

    ptcbio.com
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    Sangamo Therapeutics

    Biotechnology company developing genomic medicines for rare genetic diseases

    sangamo.com
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    Sarepta Therapeutics

    Biopharmaceutical company specializing in genetic medicine for rare diseases

    sarepta.com
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    Alnylam Pharmaceuticals

    Biopharmaceutical company developing RNAi therapeutics for rare diseases

    alnylam.com
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